X-linked lymphoproliferative disease
Showing 1 - 25 of >10,000
Acute Lymphoblastic Leukemia, Myelodysplastic Syndrome, Acute Myeloid Leukemia Trial in Houston (iCaspase9-transduced T cells,
Active, not recruiting
- Acute Lymphoblastic Leukemia
- +9 more
- iCaspase9-transduced T cells
- AP1903
-
Houston, Texas
- +1 more
Jul 22, 2022
Immune Deficiency Disorders, Severe Combined Immunodeficiency, Chronic Granulomatous Disease Trial in Saint Louis (Transplant
Recruiting
- Immune Deficiency Disorders
- +13 more
- Transplant preparative regimen of alemtuzumab, fludarabine, thiotepa, and melphalan
-
Saint Louis, MissouriWashington University
Apr 25, 2022
Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,
Recruiting
- Bone Marrow Failure Syndrome
- +15 more
- Thiotepa--single daily dose
- Thiotepa--escalated dose
-
Gainesville, FloridaUF Health Shands Children's Hospital
Jul 8, 2021
Severe Combined Immunodeficiency Disease, X-linked Trial in San Francisco, Memphis, Seattle (genetic, drug, device)
Recruiting
- Severe Combined Immunodeficiency Disease, X-linked
- CL20-i4-EF1α-hγc-OPT
- +2 more
-
San Francisco, California
- +2 more
Jan 9, 2023
Burden of Disease and Functional Impairment in XLH
Recruiting
- X Linked Hypophosphatemia
- no intervention
-
Wuerzburg, GermanyOrthopedic Center for Musculoskeletal Research, Orthopedic Depar
Aug 30, 2022
Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and
Recruiting
- Granuloma
- +4 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 25, 2023
Chronic Granulomatous Disease X-linked (X-CGD) Trial in Rome, Milan (Ibuprofen, Myelostim, Mozobil)
Recruiting
- Chronic Granulomatous Disease X-linked (X-CGD)
- Ibuprofen
- +2 more
-
Rome, Lazio, Italy
- +1 more
Oct 27, 2022
EBV-Related Hodgkin Lymphoma, Lymphoproliferative Disorders, EBV Related Non-Hodgkin's Lymphoma Trial in Houston (Dose Level 1A:
Not yet recruiting
- EBV-Related Hodgkin Lymphoma
- +2 more
- Dose Level 1A: 2 x 10^7 cells/m2
- +4 more
-
Houston, Texas
- +1 more
Feb 7, 2022
Development of Non-Invasive Prenatal Diagnosis for Single Gene
Not yet recruiting
- Invasive PreNatal Diagnosis in a Context of Family History of Single-gene Disorders, Including
- +14 more
- Blood sample
-
Paris, FranceHôpital Cochin, Maternité Port-Royal, service de Gynécologie obs
Nov 24, 2023
Evaluation of Patients With Immune Function Abnormalities
Recruiting
- Chronic Granulomatous Disease (CGD)
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 24, 2022
X-linked Hypophosphatemia Disease Monitoring Program
Active, not recruiting
- X-linked Hypophosphatemia
- Hypophosphatemic Rickets
- No intervention
-
Birmingham, Alabama
- +38 more
Dec 7, 2022
X-Linked Chronic Granulomatous Disease Trial in Paris (X vivo gene therapy)
Active, not recruiting
- X-Linked Chronic Granulomatous Disease
- X vivo gene therapy
-
Paris, FranceHôpital Necker Enfants Malades
May 20, 2021
Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar
Recruiting
- Spinal and Bulbar Muscular Atrophy
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 27, 2023
X-Linked Chronic Granulomatous Disease Trial in London (X vivo gene therapy)
Active, not recruiting
- X-Linked Chronic Granulomatous Disease
- X vivo gene therapy
-
London, United Kingdom
- +1 more
May 20, 2021
Acute Lymphoblastic Leukemia, Non Hodgkins Lymphoma, Myelodysplastic Syndrome Trial in Houston (drug, biological, radiation,
Hepatic Function in Spinal and Bulbar Muscular Atrophy
Completed
- Spinal and Bulbar Muscular Atrophy (SBMA)
- Motor Neuron Disease
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Aug 17, 2022
ALS, PLS, MND (Motor Neurone DIsease) Trial in Italy, United States
Recruiting
- ALS
- +5 more
-
Gainesville, Florida
- +8 more
Jul 20, 2023
Muscular Dystrophies, Muscular Dystrophy, Duchenne, Muscular Disorders, Atrophic Trial in Little Rock, Sacramento, Atlanta
Recruiting
- Muscular Dystrophies
- +7 more
- CAP-1002
- Placebo
-
Little Rock, Arkansas
- +9 more
Jan 9, 2023
COVID-19 Vaccine Responses in PIDD Subjects
Recruiting
- X-linked Agammaglobulinemia
- +6 more
-
Saint Petersburg, Florida
- +2 more
Apr 7, 2022
Amyotrophic Lateral Sclerosis, Kennedy Disease Trial in Paris (Muscle biopsy)
Not yet recruiting
- Amyotrophic Lateral Sclerosis
- Kennedy Disease
- Muscle biopsy
-
Paris, FrancePitié-Salpêtrière Hospital
Oct 28, 2021
Rett Syndrome, Rett Syndrome, Atypical, Genetic Disease Trial in United States
Recruiting
- Rett Syndrome
- +9 more
-
Birmingham, Alabama
- +13 more
Jul 12, 2022
Epstein-Barr Virus+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD), Solid Organ Transplant Complications,
Recruiting
- Epstein-Barr Virus+ Associated Post-transplant Lymphoproliferative Disease (EBV+ PTLD)
- +4 more
- tabelecleucel
-
Duarte, California
- +70 more
Jun 23, 2022
ESRD, Fabry Disease, Rare Diseases Trial in Boston
Terminated
- ESRD
- +5 more
-
Boston, MassachusettsMassachusetts General Hospital
Feb 22, 2021
Bipolar Disorder, Bipolar Depression, Bipolar I Disorder Trial in Stockholm (Aerobic Physical Exercise, Relaxing Physical
Not yet recruiting
- Bipolar Disorder
- +5 more
- Aerobic Physical Exercise
- +2 more
-
Stockholm, SwedenRegion Stockholm, Psykiatri Sydväst (Psychiatric Clinic Psychiat
Apr 26, 2022
Natural History Study for Charcot Marie Tooth Disease
Recruiting
- Charcot-Marie-Tooth Disease
- +47 more
-
New York, New YorkHereditary Neuropathy Foundation
Jun 12, 2023